SupplementCystic Fibrosis Foundation Evidence-Based Guidelines for Management of Infants with Cystic Fibrosis
Section snippets
Methods
The CF Foundation convened a group of experts to identify issues in the care of infants with CF and commissioned an evidence review from Johns Hopkins University. Details of this evidence review, including methods and results, are provided in the accompanying article.1 Committee members assessed this evidence in developing recommendation statements and, where possible, made evidence-based recommendations. Recommendations were graded using the United States Preventive Health Services Task Force
Conclusion
Newborn screening offers the opportunity to significantly improve the health of individuals with CF, enabling pre-symptomatic monitoring and treatment when needed to prevent or delay nutritional and pulmonary decline. Although infants with CF may appear well, subtle changes occur early in life. Rigorous and careful monitoring and timely medical intervention will permit the best possible outcome for individuals diagnosed with CF in infancy.
Author Disclosures
Drucy Borowitz, MD, has served as a consultant for Solvay Pharmaceuticals. Stephanie D. Davis, MD, has served as a consultant for Inspire Pharmaceuticals. Frank J. Accurso, MD, has received funding from Digestive Care, Inc., Axcan Pharma, and Yasoo Health, Inc. The following authors declare no financial arrangement or affiliation with a corporate organization or a manufacturer of a product discussed in this supplement: Philip M. Farrell, MD, PhD, Bruce C. Marshall, MD, Richard B. Parad, MD,
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Please see the Author Disclosures at the end of this article.